I can extract side effects

Eagle Country, Xincun City, a sunny weekend.

Singers opened the medical website he frequented, and a headline immediately came into view.

"China's leading pharmaceutical company Sanqing claims to have developed a gene drug to treat Menkes' disease!"

"The drug uses the first-generation gene editing tool ZFN to successfully knock out the key position on the mutated gene, so as to achieve the goal of completely curing the patient..."

Singers was stunned for a moment, and it took him a while to react. After reading the news in one breath, he rushed out of the study with great excitement, and found his wife who was taking care of his daughter in the bedroom.

"Honey, guess what I discovered? A pharmaceutical company in Huaxia has developed a gene drug that can cure Menkes' disease. Our daughter is saved!"

"God, do you know what you're talking about?"

"I swear, all of this is true. I saw on the news that this drug has started clinical trials in China, and there have been cases where patients have been cured. Yes, they are using gene editing treatments that can Cure this damn disease once and for all.”

"Ah, that's great, it's a miracle! Contact this pharmaceutical company quickly, our daughter can't wait."

"Okay, I will contact this pharmaceutical company right away, you wait for my good news."

Singers' daughter, who also suffers from Menkes syndrome, was given an early death notice by doctors.

But just like most family members of patients, they did not give up easily, but tried their best to save themselves.

Singers is not an ordinary person. He is the founder of a famous Wall Street hedge fund, managing assets of more than 3 billion U.S. dollars. He was once a partner of Goldman Sachs, and his wife is also a banker.

The two established a charitable organization called the Menkes Foundation with their own contribution of 10 million US dollars a year ago. The wife serves as the chairman of the foundation and is committed to funding research on this disease.

The foundation's goal is to find a cure for their daughter, and the 800 other Menkes children, before it's too late.

The couple kept in contact with powerful biopharmaceutical companies, hoping to provide interested companies with a considerable amount of research funding to promote the development of drugs targeting Menkes.

However, even with such strong financial resources and connections, things are still much more difficult than they imagined.

At an annual biology meeting, they invited seven CEOs of pharmaceutical companies to dinner, but only two came.

Even the two bosses who came here just looked at the face of these two famous bankers, and didn't have any idea of ​​research and development in this area.

It is no wonder that these pharmaceutical companies are not interested. The number of patients is too small. Even if tens of millions of charitable funds can be raised to carry out research, the potential sales of this drug are too small, and the cost cannot be recovered at all.

After some hard work, Singers was almost desperate.

Later, he found that he could not impress the pharmaceutical companies, so he funded some university laboratories and invited experts in related fields to conduct research. However, at this time, he no longer had much hope, and he was completely determined to do his best.

However, they never expected that just when they were on the verge of giving up.

Surprisingly, I saw the news that a Chinese pharmaceutical company is spontaneously researching rare disease drugs, and has actually developed a gene drug that can completely cure Menkes.

This is undoubtedly good news from heaven, and the intense emotions between the two erupted instantly.

After a heated discussion, Singers contacted Sanqing Pharmaceutical in the name of the foundation.

After some detailed inquiries, the existence of the gene medicine was finally confirmed. The two were instantly excited and hugged each other tightly, feeling the huge impact of the miracle.

However, it is a pity that Sanqing's drug is still undergoing clinical trials, and there is no clear time to market it, let alone overseas.

This is not a problem for a high-end person like Singers with strong social energy.

He quickly expressed the foundation's strong interest and expressed his willingness to fully fund overseas clinical trials of the drug.

Originally, according to Weikang's intention, Menkes' gene medicines have almost cured domestic patients after clinical trials, and there is not much motivation to start overseas phase III clinical trials immediately. After all, it is expensive and time-consuming, so there is no need to rush for a while.

But if there are local tyrants sponsoring it, it's another matter.

So he happily agreed to the request of the family of the local tycoon, and conducted the third phase of the clinical trial overseas.

With the promotion of Menkes Foundation of Singers, the application of Sanqing Overseas Branch to the FDA for Phase III clinical trials is also quite smooth.

In fact, Eagle Country is also very encouraging for rare disease drugs, providing policy incentives and fast application channels for R\u0026D companies in this area, including a 7-year market exclusivity period, tax reduction and exemption and registration application fees and other policies.

So not long after, under the golden bullet offensive of the foundation, overseas clinical trials of Menkes syndrome began, and dozens of patients became the first batch of lucky ones.

The daughter of the Singers couple finally received the life-saving medicine as she wished.

This is another heart-touching overseas version of the story of "There is no way to seek medicine, and the old father tried his best to save his daughter and save himself".

Of course, Weikang did not forget to seize this good opportunity to promote Longtu APP overseas.

Singers and other family members of children who participated in the clinic downloaded and installed the English version from the fruit and Google app stores.

After some trials, Singers widened his eyes in surprise.

"Oh my god, this, this is more amazing and potential than Menkes' gene medicine, and it is, without a doubt, what I imagine the future of medicine will look like."

"Damn it, why does Huaxia's company take the lead every step of the way, leaving Eagle Country's company far behind."

"Unfortunately, Sanqing does not accept investment from Wall Street. However, I can completely replicate his business model in Eagle National United Pharmaceutical Company. This will definitely be the best investment I have ever made in my life."

*****

In China, with the smooth progress of Menkes' clinical trials, 60 patients have been treated, and their condition has been relieved immediately. As long as the injections are continued every three months, it is believed that they will be completely cured soon.

Sanqing United Media made a documentary about the whole process from Cao Yang's visit to the research and development process of the gene drug until the treatment of these patients.

"The Choice of Things: The Story of Gene Editing"

As soon as the documentary was released, it became popular all over the Internet, and the ratings of major websites were as high as 9.8, making it comparable to "A Bite of China".

The Longtu APP also made a strong appearance in the film, and became popular all over the Internet along with the documentary.

Every audience noticed the significance of this software to patients with rare diseases, and out of curiosity, they downloaded it one after another.

Although they don't need functions such as clinical trial application and shared laboratory, electronic cases are still very practical for most people.

Users can record their own health data, take a photo of the inspection report after seeing the doctor, and then a complete data table can be formed, and evaluations and suggestions can be made on the health status.

There are also detailed medical information in the forum, which is also an excellent function for those who want to seek medical advice.

At least for them, this is an authoritative medical forum, and they can quickly get satisfactory answers to the system if they ask some common diseases.

There is no need to worry about the frightening result that cancer starts with a random search on Qiandu.

This wave of advertisements played well, and the downloads of Longtu's APP immediately began to soar.

And Sanqing also officially announced the existence of Longtu APP, and spared no effort to promote it to patients with rare diseases on the whole network.

Wei Kang has great ambitions, and he has enough strength to support this ambition.

That is, to unite all rare disease patients across the country and completely become a member of medical big data.